Hereditary Optic Neuropathy

Hereditary Optic Neuropathy

Hereditary optic neuropathies are genetic disorders that cause vision loss. Those affected may also experience cardiac or neurological abnormalities. Currently, there are no effective treatments or cures for these inherited diseases.   Optic neuropathy is one of the...
Breaking News: First Therapeutic Gene Therapy to Treat an Inherited Neuropathy is Approved for Clinical Trial!

Breaking News: First Therapeutic Gene Therapy to Treat an Inherited Neuropathy is Approved for Clinical Trial!

The first disease community to receive a therapeutic gene to the spinal cord for an ultra rare inherited neuropathy is Giant Axonal Neuropathy (GAN). Congratulations to Hannah’s Hope Fund (HHF), a 501(c)3 public charity, which has driven this collaborative research in less than six years. Six million dollars has been raised to date to fund pre-clinical and clinical research on this rare disease.

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