CMT & COVID-19

Our mission is to increase awareness and accurate diagnosis of Charcot-Marie-Tooth (CMT) and related inherited neuropathies, support patients and families living with CMT, and fund research that will lead to treatments and cures.

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Latest News From HNF

$61,000 Raised to Support Pediatric CMT Trials

Last summer HNF teamed up with the Penn Medicine Orphan Disease Center (ODC) for the Million Dollar Bike Ride (MDBR) in Philadelphia. Our fundraising goal of over $30k was achieved and matched by the ODC, granting HNF over $60k to allocate to CMT research. Thanks to...

Pharnext Announces PXT3003 for the Treatment of Charcot-Marie-Tooth Disease Type 1A has Been Granted Promising Innovative Medicine (PIM) Designation by UK Medicines and Healthcare Products Regulatory Agency

PARIS, France, 8:30 a.m., March 18, 2020 (CET) – Pharnext SA (FR0011191287 - ALPHA), a biopharmaceutical company pioneering a new approach to developing innovative drug combinations based on big genomics data and artificial intelligence, today announced that the...

Pharnext raises € 7.7 million in a private placement

PARIS, France, 08:30 a.m., March 05, 2020 (CET) – Pharnext SA (FR0011191287 - ALPHA) (the “Company”), a biopharmaceutical company pioneering a new approach to developing innovative drug combinations based on its PLEOTHERAPY artificial intelligence platform harnessing...

ACE-083 did not achieve statistically significant improvements in functional endpoints relative to placebo; Acceleron to discontinue development of ACE-083.

CAMBRIDGE, Mass.–(BUSINESS WIRE)– Acceleron Pharma Inc. (NASDAQ:XLRN), a biopharmaceutical company dedicated to the discovery, development, and commercialization of TGF-beta superfamily therapeutics to treat serious and rare diseases, today announced that treatment...

The Hereditary Neuropathy Foundation’s Movement is Medicine™ Program Expands to Florida and Continues to Shed Light on the Impact Exercise Has on Charcot-Marie-Tooth (CMT)

NEWS PROVIDED BY Hereditary Neuropathy Foundation Mar 03, 2020, 06:03 ET NEW YORK, March 3, 2020 /PRNewswire/ -- The Hereditary Neuropathy Foundation (HNF) Movement is Medicine™ is expanding across the US with its latest Summit announced for March 21,...