November 5, 2023
Runners will take on the marathon to support CMT research.
If you are interested in participating please email [email protected].
November 5, 2023
Runners will take on the marathon to support CMT research.
If you are interested in participating please email [email protected].
On Friday, September 28, 2018 HNF hosted an Externally-led Patient Focused Drug Development (PFDD) Meeting. In attendance were patients, caregivers, Government Officials, Healthcare Providers, Industry Representatives, and Payors.
This study is a new international research project funded by the National Institutes of Health (NIH) called Accelerate Clinical Trials in Charcot-Marie-Tooth Disease (ACT-CMT).
Helixmith, specializing in gene therapy research for over 20 years, has kicked off its phase I and 2a clinical trial for using VM202 (Engensis) to treat CMT1A.
US Food and Drug Administration has agreed with Pharnext and provided clear guidance on the regulatory pathway to approval for PXT3003, including key design elements of a single pivotal Phase III study
treatment with ACE-083 in patients with Charcot-Marie-Tooth disease (CMT) did not demonstrate functional improvement in the Phase 2 trial
Welcome and Opening Remarks Overview: What is CMT? - Michael Shy, MD Overview: What is CMT? - Dr....
HNF successfully executed the Externally-led PFDD Meeting for the FDA on September 28th, 2018.
HNF will be holding a landmark externally-led Patient-Focused Drug Development Meeting for CMT and INs in Washington, D.C. on Friday, September 28, 2018.
2018 will be “the year” for our community as we prepare for the externally-led Patient-Focused Drug Development Meeting.
Help support this ground-breaking PFDD CMT Meeting being held on September 28, 2018 in Washington, D.C.
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