Participating in a clinical trial is an invaluable way to get involved in helping the research community cure Charcot-Marie-Tooth (CMT) and related inherited neuropathies (INs). There are various types of clinical trials. Clinical trials are sometimes referred to as clinical studies or clinical research involving human volunteers that have been Food and Drug Administration (FDA) and European Medicines Agency (EMA) approved, the regulatory agencies for the U.S. and Europe. These agencies require that a potential therapy be extensively tested in large groups of human volunteers before it can receive approval for commercialization.

Clinical trials are a vital part of the scientific research process and essential for developing therapies to prevent, treat, reverse and cure CMT. There are several types of clinical trials currently being conducted for CMT.

If you don’t find a clinical trial below, please visit HNF’s Centers of Excellence for more information or contact us for assistance.