PFDD Meeting Sessions

by | Dec 19, 2018 | 0 comments

Welcome and Opening Remarks

Overview: What is CMT? – Michael Shy, MD

Overview: What is CMT? – Dr. Stephan Züchner, MD, PhD

Goals & Objectives for the Meeting, Participant Polling of Demographic Questions

Session 1: Symptoms and Daily Challenges for Pediatrics & Young Adults

Session 2: Symptoms and Daily Challenges for Adults Living with CMT

Session 3: Current and Future Approaches to Treatments

Pipeline Overview Therapies in Development – Florian Thomas, MD, MA, PhD, MS

Summary from FDA & Closing Remarks

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PFDD Meeting, September 28, 2018

PFDD Meeting, September 28, 2018

On Friday, September 28, 2018 HNF hosted an Externally-led Patient Focused Drug Development (PFDD) Meeting. In attendance were patients, caregivers, Government Officials, Healthcare Providers, Industry Representatives, and Payors. 

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