Brews & Bingo For CMT

The Externally-led Patient-Focused Drug Development (PFDD) Meeting Was A Huge Success!

by Courtney | Dec 5, 2018 | PFDD | 0 Comments

HNF successfully executed the Externally-led PFDD Meeting for the FDA on September 28th, 2018.

HNF’s Landmark Externally-Led Patient-Focused Drug Development Meeting

by Courtney | Apr 13, 2018 | PFDD Meeting 28SEP2018 | 0 Comments

HNF will be holding a landmark externally-led Patient-Focused Drug Development Meeting for CMT and INs in Washington, D.C. on Friday, September 28, 2018.

HNF’s Roadmap To Clinical Trial Development

by Allison Moore | Mar 16, 2018 | Clinical Trials | 1 Comment

2018 will be “the year” for our community as we prepare for the externally-led Patient-Focused Drug Development Meeting.

Landmark “Voice of the Patient” PFDD CMT Meeting Needs All Hands on Deck!

by Courtney | Jan 29, 2018 | PFDD Meeting 28SEP2018 | 1 Comment

Help support this ground-breaking PFDD CMT Meeting being held on September 28, 2018 in Washington, D.C.

Hope on the Horizon: CMT & FDA Patient-Focused Drug Development Meeting for Charcot-Marie-Tooth to be Held in 2018

by Allison Moore | Dec 4, 2017 | PFDD Meeting 28SEP2018 | 2 Comments

HNF will be holding a landmark externally-led Patient-Focused Drug Development (PFDD) Meeting CMT & INs in Washington, D.C. on September 28, 2018. The meeting will be held in conjunction with September National CMT Awareness Month.

Pharnext’s lead PLEODRUG © for treatment of CMT1

by Courtney | Nov 9, 2017 | Clinical Trials, CMT Type - CMT1A, Pharnext | 5 Comments

Pharnext completed patient enrollment for the international Phase 3 clinical trial of PXT3003, Pharnext’s lead PLEODRUG ©, for treatment of CMT1A.

Are You a Patient With CMT 1A? New Clinical Trial Opportunity Available For You!

by Courtney | Oct 31, 2016 | Clinical Trials, Featured | 9 Comments

For the first time investigators are looking for patients to participate in a pivotal Phase 3 clinical trial of Pharnext’s lead investigational pleodrug, PXT-3003 for the potential treatment of Charcot-Marie-Tooth Disease Type 1A (CMT1A).

Pharnext Opens First U.S. Study Site For Its PLEO-CMT International Pivotal Phase 3 Trial In Charcot-Marie-Tooth Disease Type 1A

by Courtney | Apr 25, 2016 | Clinical Trials | 7 Comments

French pharmaceutical company Pharnext announced the opening of the first U.S. trial site for its PLEO-CMT pivotal Phase 3 clinical trial of its lead pleodrug PXT-3003 in Charcot-Marie-Tooth Disease Type 1A (CMT1A).

Breaking News: First Therapeutic Gene Therapy to Treat an Inherited Neuropathy is Approved for Clinical Trial!

by Courtney | Mar 6, 2015 | Clinical Trials, CMT Type - GAN, CMT Update | 9 Comments

The first disease community to receive a therapeutic gene to the spinal cord for an ultra rare inherited neuropathy is Giant Axonal Neuropathy (GAN). Congratulations to Hannah’s Hope Fund (HHF), a 501(c)3 public charity, which has driven this collaborative research in less than six years. Six million dollars has been raised to date to fund pre-clinical and clinical research on this rare disease.

Positioning HNF to Translate Treatments to Clinical Trials

by Courtney | Dec 9, 2014 | Clinical Trials, CMT Update | 0 Comments

In June 2013, HNF made the important decision to refine the organization’s mission. We now place more importance on new initiatives that take our research discoveries and translate them to the next phase in the drug discovery process.

We divide our research initiatives into 3 areas:

WHAT IS CMT

TYPES OF CMT

PATIENT RESOURCES

CMT UPDATES

CMT CONNECT

CMT Research

TRIAD

GRIN PATIENT REGISTRY

PEDIATRICS & CMT

WHAT IS MITO

TYPES OF MITOS

MITO Faces

MITO Research

TRIAD - Mito

GRIN PATIENT REGISTRY

PEDIATRICS & MITO CMT

FDA

CLINICAL TRIALS

PATIENT-FOCUSED RESEARCH

EMERGING TECHNOLOGIES

GENETIC TESTING - CMT GENIE

MOVEMENT IS MEDICINE™

FACES OF CMT

INDUSTRY

HCPs/CENTERS OF EXCELLENCE

RESEARCH FUNDING

About HNF

OUR STORY

FOUNDATION LEADERSHIP

990's & ANNUAL REPORTS

Join Team CMT

Ways to Give

Amazon Wishlist

CMT Shop

GRIN Registry

Facebook Fundraiser

Celebrate your birthday with a purpose

Participate or Host an event

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