"Voice of the Patient"
Calling ALL kids up to 18 years old with CMT
Kids needed for a video conference focus group for
HNF’s Externally-led Patient-Focused Drug Development (PFDD) Meeting
We are looking for kids that would be willing to participate in a video conference focus group. The purpose of the focus group is to hear from you what it’s like to live with CMT and to help us gather patient reported data to prepare for the Externally-led Patient Focused Drug Development (PFDD) Meeting.
The focus group will last 90 minutes. The meeting will have a moderator to facilitate questions and encourage interactive dialogue. We encourage parents to be present.
The PFDD meeting is an opportunity for patients and families to inform the FDA, drug developers and other key stakeholders, on the true burdens of living with CMT and how patients view the benefits and risks of treatments for CMT.